xFrench gene therapy success
A report in last week's New England Journal of Medicine shows that children treated by gene therapy at the Necker Hospital for Sick Children in Paris, France, are still living normal lives after more than two years. Four boys were successfully treated in the French study, all having the X-linked...
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Success stories in gene therapy
by Dr Jess Buxton
After over a decade of largely unsuccessful clinical trials, the persistence of gene therapy researchers is finally beginning to pay off. Two weeks ago came news of the remarkable recovery made by Rhys Evans, the UK toddler who underwent gene therapy to treat an inherited immune system disorder. The scientists...