FDA opens path to approval for Hunter syndrome gene therapy
The US Food and Drug Administration is allowing biotech company Regenxbio to reapply for licensing of a gene therapy for Hunter syndrome, in a reversal of its previous decision...
Rebecca Simkin is a Volunteer Writer at BioNews, having joined the publication through its writing scheme. She is a PhD student at University College London (UCL) and works in the laboratory of Professor Pietro Fratta. Her research focuses on models of amyotrophic lateral sclerosis and aims to determine how disease-associated mutations contribute to neuromuscular junction susceptibility. She previously obtained a BSc in Pharmacology from the University of Bristol and an MRes in Translational Neuroscience from UCL. Alongside her research, Rebecca is interested in science communication and uses imaging to make her work more engaging and accessible to wider audiences. Her scientific images have been recognised through competitions hosted by FocalPlane and the UCL Doctoral School.
The US Food and Drug Administration is allowing biotech company Regenxbio to reapply for licensing of a gene therapy for Hunter syndrome, in a reversal of its previous decision...
The birth parents of a baby born after an IVF embryo mix-up will retain permanent custody under a court agreement with the genetic parents...
Early results from an ongoing Phase I clinical trial suggest that a single dose of CAR T-cell therapy may benefit patients with severe, treatment-resistant lupus...
Overproduction of a DNA repair protein called EXO1 can trigger DNA damage and increase chemotherapy sensitivity in human cancer cells, a new study has reported...
Reviewing It's the Hope that Kills You, Rebecca Simkin praises Tim Royle's sensitive and understated approach to IVF, highlighting the film's emotional honesty and its thoughtful focus on male underrepresentation within fertility treatment...
Testicular tissue preserved before puberty shows signs of being capable to create sperm after being grafted back into the same patient in adulthood, a proof-of-concept study reports...
A refined method has been developed to generate more mature, functional stem-cell-derived pancreatic islets that restore and maintain glucose control in diabetic mice over several months...
Men with severely reduced fertility have a greater likelihood of developing certain non-reproductive cancers, new research suggests...
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