BioNews
NHS should adopt gene therapies faster, says industry body
The NHS must adopt new budget strategies to research and manufacture cell and gene therapies of the future, according to a recent report...
NICE recommends Casgevy for treatment of severe beta-thalassaemia
A new gene therapy, Casgevy, has been recommended for use on the NHS in England for people living with a severe form of beta-thalassaemia...
Gene therapy stops, and may reverse, muscular dystophy in mice
A gene therapy for Duchenne muscular dystrophy has halted the muscle decline associated with the condition in mice, and has also shown promise at repairing the muscles...
Stem cell transplant recipients can have successful pregnancies
Some women can become pregnant and give birth to healthy children after undergoing stem cell transplantation, according to a new retrospective study...
NHS funding approved for haemophilia B gene therapy
A new gene therapy for haemophilia B is to be made available for NHS patients after approval from the UK's National Institute for Health and Care Excellence.
Genome editing of lung stem cells treats cystic fibrosis in mice
A CRISPR genome-editing therapy has been shown for the first time to provide long-term genome correction in lung cells for treatment of cystic fibrosis in mice...
Gene therapy restores hearing in both ears of children with rare genetic deafness
A gene therapy has restored hearing in five children, marking the first successful treatment in both ears following earlier single-ear trials...