BioNews
Two gene therapies for deafness make progress
A long-term clinical trial of a gene therapy for a rare genetic form of deafness has demonstrated sustained hearing restoration, while a separate gene therapy for the same condition has received approval from the Food and Drug Administration...
Child's sight improves following gene therapy for blindness
A child born with a congenital retinal disorder has had her sight restoredby an NHS-funded gene therapy...
Gene therapy pioneers win major science prizes
Breakthrough Prizes in Life Sciences have been awarded to two teams of scientists for their work on gene therapies for inherited blood and blindness conditions...
mRNA treatment helps infertile mice produce sperm
Delivery of messenger RNA into the testes of infertile mice can reactivate spermatogenesis...
Spotting the zebras among the horses: Understanding metabolic disorders
Metabolic disorders can seem forbiddingly complex, but a simplified approach to explaining their biological basis can lead to improved understanding, earlier diagnosis and better management, argues Dr Srividya Sreekantam...
New approach to delivering gene therapy for cystic fibrosis
A lipid nanoparticle-based gene therapy for cystic fibrosis restores biological function in a preclinical model...
