CRISPR gene therapy for sickle cell approved for NHS use
Gene therapy, Casgevy, has been recommended for use on the NHS in England for some people living with a severe form of sickle cell disease...
Gene therapy, Casgevy, has been recommended for use on the NHS in England for some people living with a severe form of sickle cell disease...
A novel gene insertion therapy may be able to cure infants of a rare genetic liver disease...
Elevidys, a gene therapy for Duchenne muscular dystrophy, remains under review in the EU and the UK...
Gene therapy reversed heart failure and restored normal heart function, in a study on minipigs...
A new one-time gene therapy has prevented bleeding episodes in haemophilia A patients in an investigational study carried out in India...
A molecule that can be used to enhance CRISPR genome editing also causes unintended destruction of large sections of the genome in human cells...
The High Court has held that a patent owned by uniQure for the treatment of haemophilia B is valid and was infringed by Pfizer...
A novel gene therapy approach that directly targets immune cells within a patient's body has been trialled in a B-cell cancer patient...
Artificial intelligence methods have produced simulated DNA to determine gene expression, a new study has revealed...
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