Podcast Review: How Gene Therapy is Offering Hope – Once Again
The past, present and future of gene therapies is discussed in this Pulse podcast...
by Olivia Goff
The past, present and future of gene therapies is discussed in this Pulse podcast...
Two gene therapies for the treatment of sickle cell disease have been approved by the US Food and Drug Administration...
by BioNews
Adults with thalassemia, a severe genetic blood disorder, will be offered potentially curative stem cell transplants on the NHS for the first time...
by Yan Lau
A gene therapy treatment for sickle cell disease has led to a build-up of cells with genetic mutations that make them grow faster, increasing blood-cancer risk, researchers revealed...
by Olivia Goff
CRISPR base editing therapy reduced cholesterol levels in the blood of a small cohort of patients, clinical trial interim data has shown...
A CRISPR-based treatment for sickle cell disease is one step closer to approval after an advisory committee for the US Food and Drug Administration met to review its safety...
by Yan Lau
A gene therapy trial in China has restored hearing in children born with a rare genetic form of deafness...
A world-first trial has launched in the UK to see whether gene therapy can provide hearing for children with severe to profound hearing loss caused by a rare genetic condition...
The US Food and Drug Administration's Advisory Committee for Cellular, Tissue and Gene Therapies has voted that there is insufficient evidence that experimental stem-cell therapy for ALS is effective enough to warrant approval by the agency...
BioNews, published by the Progress Educational Trust (PET), provides news and comment on genetics, assisted conception, embryo/stem cell research and related areas.