Rare genetic disease appears to be cured after gene therapy
A novel gene insertion therapy may be able to cure infants of a rare genetic liver disease...
A delivery system used in the laboratory to carry foreign DNA into a cell. Modified viruses are commonly used as vectors in gene therapy.
A novel gene insertion therapy may be able to cure infants of a rare genetic liver disease...
A new one-time gene therapy has prevented bleeding episodes in haemophilia A patients in an investigational study carried out in India...
A novel gene therapy approach that directly targets immune cells within a patient's body has been trialled in a B-cell cancer patient...
A gene therapy for Duchenne muscular dystrophy has halted the muscle decline associated with the condition in mice, and has also shown promise at repairing the muscles...
A personalised form of genome-edited T cell therapy has shown promising results for the treatment of solid tumours...
Gene therapy has partly restored colour detection in two children that were born totally colour blind...
A new method of gene therapy has shown initial success in treating patients with the bleeding disorder haemophilia B...
A baby has become the first NHS patient to receive gene therapy for spinal muscular atrophy...
The NHS has agreed a deal to make gene therapy available for children with spinal muscular atrophy...
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