Gene therapy temporarily halts type 1 diabetes in mice
A gene therapy has been used to restore normal blood sugar levels in mice with type 1 diabetes, according to a study published this month in the journal Cell Stem Cell.
BioNews
Vector
A delivery system used in the laboratory to carry foreign DNA into a cell. Modified viruses are commonly used as vectors in gene therapy.
96 articles
Gene therapy shows 'mind-blowing' success in treating haemophilia A
A new gene therapy for haemophilia A has exceeded expectations in a recent clinical trial...
New CRISPR technique reverses diabetes and kidney failure in mice without cutting DNA
Scientists in California have used a modified form of the CRISPR/Cas9 genome editing approach to epigenetically treat diabetes, kidney disease and muscular dystrophy in mice...
Sick boy gets healthy new skin with genetically-altered stem cells
A boy with a rare skin disease has been successfully treated by replacing most of his skin with grafts of stem cells modified by gene therapy.
FDA advisors back gene therapy for rare inherited blindness
The US Food Drug and Administration advisory committee has backed the use of gene therapy to treat a hereditary disease for the first time...
'CRISPR-Gold' repairs muscular dystrophy gene in mouse model
Scientists have repaired the faulty gene in a mouse model of muscular dystrophy by using gold nanoparticles to deliver the genome editing tool CRISPR-Cas9...
Image by Peter Artymiuk via the Wellcome Collection. Depicts the shadow of a DNA double helix, on a background that shows the fluorescent banding of the output from a DNA sequencing machine.
Gene therapy restores vision in blind mice
Gene therapy has restored some vision in mice blinded by retinitis pigmentosa, an inherited degenerative eye disease...
Gene therapy reverses multiple sclerosis in mice
A novel gene therapy can reverse the symptoms and progression of disease in a mouse model of multiple sclerosis...
Gene therapy skin grafts for obesity and diabetes
A proof-of-concept study in mice has demonstrated how skin grafts could deliver gene therapy for obesity and diabetes...
Image by Peter Artymiuk via the Wellcome Collection. Depicts the shadow of a DNA double helix, on a background that shows the fluorescent banding of the output from a DNA sequencing machine.
Gene therapy reverses muscular dystrophy in dogs in world first
A safe and effective gene therapy treating Duchenne muscular dystrophy in dogs has been demonstrated...